Beam's BEAM-301: 2/3 GSD1a patients off corn starch after single base-editing dose
IAmSamFin · x · 2026-10-27
Beam Therapeutics shared full data for BEAM-301 in GSD1a across the first two dose cohorts. Notably, 2 of 3 patients at the second dose level achieved maximum fasting duration and no longer require corn starch supplementation after a single dose of the in-vivo base editor.
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